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Research Studies

Research Studies

UCD Consortium NIH Office of Rare Diseases-sponsored Research Studies

Completed Studies

Industry (Pharmaceutical Company) Sponsored Clinical Trials

If you have questions or would like to discuss any of the studies or clinical trials, please contact NUCDF at

“I have been a participant or observer in many efforts to bring together families and researchers in regard to a specific disorder or group of disorders, and I have never seen one in which there was such a superb collaboration and focus on the common goal.” 

Hugo Moser, M.D., Adrenoleukodystrophy Researcher (“Lorenzo’s Oil”), Kennedy-Krieger Institute, NIH Monitor to UCDC